Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy

Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy

THE NEW ENGLAND JOURNAL OF MEDICINE Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy Published February 19, 2025 | DOI: 10.1056/NEJMc2300802 | Copyright © 2025 Abstract The alternate splicing small molecule risdiplam, administered to a fetus with spinal...
A newly identified macrophage manager ZEB2

A newly identified macrophage manager ZEB2

A newly identified macrophage manager ZEB2: still known as pivotal in early fetal development and cancer progression by driving the epithelial-to-mesenchymal transition. Now proven as a master switch controlling the tumor-associated macrophage program Fadi Sheban ,...